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Jazz Pharmaceuticals defitelio defitelio defibrotide
Defitelio Defitelio Defibrotide, supplied by Jazz Pharmaceuticals, used in various techniques. Bioz Stars score: 86/100, based on 1 PubMed citations. ZERO BIAS - scores, article reviews, protocol conditions and more
https://www.bioz.com/product/defitelio/pm40207986-425-0-5?v=Jazz+Pharmaceuticals
Average 86 stars, based on 1 article reviews
defitelio defitelio defibrotide - by Bioz Stars, 2026-08
86/100 stars

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Compilation of approved nucleic acid drugs

Journal: Clinical and Experimental Medicine

Article Title: Advances in nucleic acid therapeutics: structures, delivery systems, and future perspectives in cancer treatment

doi: 10.1007/s10238-024-01463-4

Figure Lengend Snippet: Compilation of approved nucleic acid drugs

Article Snippet: Defibrotide (Defitelio) , Hepatic veno-occlusive disease , ASO , / , Jazz Pharmaceuticals , 2016.

Techniques: Vaccines

Real‐world evidence (RWE) and other observational approaches are used to support single‐arm trials.

Journal: Clinical and Translational Science

Article Title: Real‐world evidence to support regulatory submissions: A landscape review and assessment of use cases

doi: 10.1111/cts.13903

Figure Lengend Snippet: Real‐world evidence (RWE) and other observational approaches are used to support single‐arm trials.

Article Snippet: Product: Defibrotide sodium (Defitelio), Jazz Pharmaceuticals, 2016 Therapeutic area: Non‐oncology Regulatory use type and purpose: Original marketing application approval Regulatory Agency: FDA , Efficacy/effectiveness data collection , External RWD controls (direct matching) , Retrospective RWD cohort , Site‐based chart data, Registries , Hematopoietic stem cell transplantation (HSCT) 100‐day survival rate.

Techniques: Clinical Proteomics, Biomarker Discovery, Control, Recombinant, Marker, Transplantation Assay, Emulsion, Virus

FDA-approved RNA drugs

Journal: Molecular Therapy. Nucleic Acids

Article Title: RNA therapeutics in targeting G protein-coupled receptors: Recent advances and challenges

doi: 10.1016/j.omtn.2024.102195

Figure Lengend Snippet: FDA-approved RNA drugs

Article Snippet: Defibrotide , Defitelio , adenosine A1/A2receptor , veno-occlusive disease in liver , Jazz Pharmaceuticals , 2016.

Techniques: Binding Assay